Haemophilia News

7th August 2018 Mark Ward

HAEMOPHILIA NEWS

The purpose of this page is to provide news articles related to Haemophilia.

The information contained on this page includes various items, for example:

Developments of new clotting products, vaccination updates and haemophilia industry business along with other areas of this specialist field of medicine.

Click on each link to read the News article:

August

Spark Therapeutics shares lose more than a quarter of their value as hemophilia gene therapy trial disappoints investors

A lab worker at Spark Therapeutics in Philadelphia, PA.

The Philadelphia-based company said that its treatment for hemophilia A reduced bleeds and the need for therapeutic infusions by 97 percent in a trial of 12 patients, and that it plans to start a late-stage clinical trial in the fourth quarter.

At the highest dose in the study, which the company plans to use in its phase 3 trial, five of seven patients saw levels of the protein important in hemophilia A restored to an average of 30 percent of normal, the company said when it reported second-quarter financial results.

Continue Reading:

https://www.cnbc.com/2018/08/07/spark-therapeutics-gene-therapy-reduces-bleeding-in-hemophilia-a-trial.html

July

Image result for farnham herald logo

Service honours haemophiliacs

The Treloars Former Pupils’ Association is inviting staff, pupils and friends of Treloar School and College, past and present, to join them this month for a special service at the Church of the Holy Rood in Holybourne, near Alton.

The service at the newly-refurbished church on July 28 will dedicate a new pew in memory of the haemophiliac boys who lost their lives after being given contaminated blood products

Continue Reading:

http://www.farnhamherald.com/article.cfm?id=127782&headline=Service%20honours%20haemophiliacs&sectionIs=news&searchyear=2018

NHS England says yes to Roche’s Hemlibra

Hemlibra

While NICE is England’s best known market access gatekeeper, NHS England is in direct control of specialised commissioning, and negotiates directly on pricing and reimbursement on a select number of specialised and high cost medicines.

Continue Reading:

http://www.pmlive.com/pharma_news/nhs_england_says_yes_to_roches_hemlibra_1243594

June

DWP REVIEWING PIP APPLICATIONS FROM PEOPLE WITH BLEEDING DISORDERS

In October 2017, the Department for Work and Pensions set up a working group with individuals affected by contaminated blood and blood products to hear about their experiences of the application and assessment procedures for disability benefits.

The working group highlighted issues with how claimants with haemarthropathy (a severe type of arthritis caused by bleeding into joints) were being assessed for Personal Independence Payment (PIP).

The need to review such PIP cases was identified and these reviews will begin today. No one will have their awards reduced as a result of this review.

The review will happen automatically and there is no need for people to do anything at this point, however, anyone with haemarthropathy who believes their case should be reviewed but does not receive a letter by 23rd July 2018 should phone the dedicated phone line 0800 121 4296 as soon as possible after that date.

For more information, please read the statement from the Department for Work and Pensions here.

http://haemophilia.org.uk/2018/06/25/review-of-haemarthropathy-cases-begins/